Orphan diseases are conditions that affect a small percentage of the population, typically fewer than 200,000 people in the U.S., and often face challenges in research and treatment.
Orphan drugs are pharmaceutical agents developed specifically to treat rare medical conditions, often referred to as orphan diseases.
A comprehensive guide to understanding rare diseases, their types, historical context, key events, importance, and applicability.
The Orphan Drug Credit is a U.S. tax incentive designed to help pharmaceutical companies manage the high costs associated with developing drugs and treatments for exceedingly rare diseases. This article explores its purpose, benefits, and implications.
